Case Report: Twenty years of metreleptin therapy in congenital generalized lipodystrophy type 1: the longest reported follow-up to date
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By
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Elise Van der Borght
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Bart Van der Schueren
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Roman Vangoitsenhoven
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David Cassiman
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Baris Akinci
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Rebecca J. Brown
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Elif A. Oral
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Ann Mertens
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Pieter-Jan Martens
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May 13, 2026